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Co-delivery of indoleamine 2,3-dioxygenase prevents loss of expression of an antigenic transgene in dystrophic mouse muscles
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Characterization of a novel adeno-associated viral vector with preferential oligodendrocyte tropism
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Cationic microRNA-delivering nanocarriers for efficient treatment of colon carcinoma in xenograft model
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Excision of HIV-1 DNA by gene editing: a proof-of-concept in vivo study
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Tackling chondrocyte hypertrophy with multifunctional nanoparticles
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CRISPR-on system for the activation of the endogenous human INS gene
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Adenoviral vector encoding soluble Flt-1 engineered human endometrial mesenchymal stem cells effectively regress endometriotic lesions in NOD/SCID mice
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Opposing effects of Sca-1+ cell-based systemic FGF2 gene transfer strategy on lumbar versus caudal vertebrae in the mouse
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Systemic injection of AAV9 carrying a periostin promoter targets gene expression to a myofibroblast-like lineage in mouse hearts after reperfused myocardial infarction
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Mifepristone-inducible transgene expression in neural progenitor cells in vitro and in vivo
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HSV vector-mediated GAD67 suppresses neuropathic pain induced by perineural HIV gp120 in rats through inhibition of ROS and Wnt5a
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AAV1/2-mediated BDNF gene therapy in a transgenic rat model of Huntington’s disease
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