Volume 28 Issue 7-8, August 2021

Cover Credit:Enhanced brain transduction efficiency in MPS IIIB mice with neonatal 6 site intra-parenchymal injection of a total of 1.4 x 10¹⁰ vector genomes of AAV8 triple capsid mutant expressing GFP.

Comment

Gene therapy in the CNS—one size does not fit all

Melissa R. Andrews
Comment 25 Sept 2020
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Perspective

Prime editing – an update on the field

Janine Scholefield
Patrick T. Harrison

Collections:

Reader's Choice 2021

Gene Editing
Perspective Open Access 24 May 2021

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Review Article

Gene delivery to the hypoglossal motor system: preclinical studies and translational potential

Brendan M. Doyle
Michele L. Singer
David D. Fuller
Review Article Open Access 11 Feb 2021

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Article

MiR-140-5p inhibits oxidized low-density lipoprotein-induced oxidative stress and cell apoptosis via targeting toll-like receptor 4

Huifang Liu
Ziming Mao
Fengling Chen
Article 12 Mar 2020
AAV3-miRNA vectors for growth suppression of human hepatocellular carcinoma cells in vitro and human liver tumors in a murine xenograft model in vivo

Ling Yin
Geoffrey D. Keeler
Arun Srivastava
Article 09 Mar 2020
Transduction patterns in the CNS following various routes of AAV-5-mediated gene delivery

K. L. Pietersz
R. M. Martier
B. Blits
Article 15 Aug 2020
Site-specific modifications to AAV8 capsid yields enhanced brain transduction in the neonatal MPS IIIB mouse

Janine A. Gilkes
Benjamin L. Judkins
Coy D. Heldermon
Article Open Access 26 Nov 2020
Use of CRISPR/Cas9-mediated disruption of CNS cell type genes to profile transduction of AAV by neonatal intracerebroventricular delivery in mice

Tess Torregrosa
Sydney Lehman
Shih-Ching Lo

Collections:

Editor's Choice

Gene Editing
Article Open Access 22 Feb 2021

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Correction

Correction: Conditional replication of oncolytic viruses based on detection of oncogenic mRNA

M. Renteln
Correction 07 Jan 2021
Correction: Targeted gene correction in the mdx mouse using short DNA fragments: towards application with bone marrow-derived cells for autologous remodeling of dystrophic muscle

R. M. Kapsa
A. F. Quigley
A. J. Kornberg
Correction 03 Feb 2021

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Volume 28 Issue 7-8, August 2021

Comment

Gene therapy in the CNS—one size does not fit all

Perspective

Prime editing – an update on the field

Review Article

Gene delivery to the hypoglossal motor system: preclinical studies and translational potential

Article

MiR-140-5p inhibits oxidized low-density lipoprotein-induced oxidative stress and cell apoptosis via targeting toll-like receptor 4

AAV3-miRNA vectors for growth suppression of human hepatocellular carcinoma cells in vitro and human liver tumors in a murine xenograft model in vivo

Transduction patterns in the CNS following various routes of AAV-5-mediated gene delivery

Site-specific modifications to AAV8 capsid yields enhanced brain transduction in the neonatal MPS IIIB mouse

Use of CRISPR/Cas9-mediated disruption of CNS cell type genes to profile transduction of AAV by neonatal intracerebroventricular delivery in mice

Correction

Correction: Conditional replication of oncolytic viruses based on detection of oncogenic mRNA

Correction: Targeted gene correction in the mdx mouse using short DNA fragments: towards application with bone marrow-derived cells for autologous remodeling of dystrophic muscle

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