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Gene therapy

Repair and replace

Nature volume 510, pages 226–227 (2014)Cite this article

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One approach to treating inherited diseases is repairing the defective genes, but this has proved challenging in stem cells. An optimized protocol has now been developed that allows gene repair in blood-cell precursors. See Article p.235

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Figure 1: Strategies for treating inherited diseases with gene therapy.

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Authors and Affiliations

  1. Alain Fischer is at the Imagine Institute, Hôpital Necker-Enfants Malades, Paris 75015, France, and at the Collège de France, Paris.,

    Alain Fischer

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  1. Alain Fischer
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Correspondence to Alain Fischer.

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Fischer, A. Repair and replace. Nature 510, 226–227 (2014). https://doi.org/10.1038/nature13344

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