Neurology articles within Gene Therapy

Featured

• Review | 28 July 2017

  Management of neuromuscular diseases and spinal muscular atrophy in Latin America

  • S Monges
  •  & A L Rosa

• Review
  23 July 2017 | Open Access

  The clinical landscape for SMA in a new therapeutic era

  • K Talbot
  •  & E F Tizzano

• Review | 31 May 2017

  Therapeutic approaches for spinal muscular atrophy (SMA)

  • M Scoto
  • , R S Finkel
  •  & F Muntoni

• Review | 31 May 2017

  The SMA Trust: the role of a disease-focused research charity in developing treatments for SMA

  • V Christie-Brown
  • , J Mitchell
  •  & K Talbot

• Review | 30 May 2017

  Developmental regulation of SMN expression: pathophysiological implications and perspectives for therapy development in spinal muscular atrophy

  • S Jablonka
  •  & M Sendtner

• Original Article | 29 January 2016

  Intracerebroventricular delivery of self-complementary adeno-associated virus serotype 9 to the adult rat brain

  • A Donsante
  • , Z McEachin
  •  & N M Boulis