Huntington's disease articles within Gene Therapy

Featured

• Original Article
  03 August 2017 | Open Access

  AAV5-miHTT gene therapy demonstrates suppression of mutant huntingtin aggregation and neuronal dysfunction in a rat model of Huntington’s disease

  • J Miniarikova
  • , V Zimmer
  •  & P Konstantinova

• Original Article | 24 December 2015

  AAV_1/2-mediated BDNF gene therapy in a transgenic rat model of Huntington’s disease

  • B Connor
  • , Y Sun
  •  & C Maucksch

• Original Article | 15 November 2012

  In vivo delivery of DN:REST improves transcriptional changes of REST-regulated genes in HD mice

  • P Conforti
  • , A Mas Monteys
  •  & E Cattaneo

• Short Communication | 15 March 2012

  Axonal transport of adeno-associated viral vectors is serotype-dependent

  • E A Salegio
  • , L Samaranch
  •  & K S Bankiewicz

• Review | 08 December 2011

  Using non-coding small RNAs to develop therapies for Huntington's disease

  • Y Zhang
  •  & R M Friedlander

• Short Communication | 13 May 2010

  BDNF regulation under GFAP promoter provides engineered astrocytes as a new approach for long-term protection in Huntington's disease

  • A Giralt
  • , H C Friedman
  •  & J Alberch