Featured
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Brief Communication |
Design and applications of gene therapy vectors for mucopolysaccharidosis in Colombia
- Carlos J. Alméciga-Diaz
- & Luis A. Barrera
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Original Article |
Synergistic effects of deleting multiple nonessential elements in nonreplicative HSV-1 BAC genomic vectors play a critical role in their viability
- M Ventosa
- , A Ortiz-Temprano
- & F Lim
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Original Article |
In vitro gene manipulation of spinal muscular atrophy fibroblast cell line using gene-targeting fragment for restoration of SMN protein expression
- A Rashnonejad
- , C Gündüz
- & F Özkınay
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Short Communication
| Open AccessCRISPR/Cas9 DNA cleavage at SNP-derived PAM enables both in vitro and in vivo KRT12 mutation-specific targeting
- D G Courtney
- , J E Moore
- & C B T Moore
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Original Article |
Site promiscuity of coliphage HK022 integrase as a tool for gene therapy
- M Kolot
- , N Malchin
- & E Yagil