The past 10 years have seen substantial advances in many areas of paediatric endocrinology. Major progress has been made in our understanding of the aetiology of many disorders with the advent of next-generation sequencing. Furthermore, the introduction of novel therapies has revolutionized clinical management.
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M.T.D. is funded by the Great Ormond Street Hospital Children's Charity.
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Dattani, M. New genes, new therapies. Nat Rev Endocrinol 11, 638–639 (2015). https://doi.org/10.1038/nrendo.2015.154
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DOI: https://doi.org/10.1038/nrendo.2015.154