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Gene therapies for rare diseases are under threat. Scientists hope to save them

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doi: https://doi.org/10.1038/d41586-023-03109-z

Updates & Corrections

  • Correction 06 October 2023: An earlier version of this article misstated P. J. Brooks’s title.

  • Correction 09 October 2023: The original title given for P. J. Brooks was, in fact, correct. The story has been updated accordingly.

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