Transcription articles within Gene Therapy

Featured

• Article | 12 December 2022

  An ectopic enhancer restores CFTR expression through de novo chromatin looping

  • Jenny L. Kerschner
  • , Alekh Paranjapye
  •  & Ann Harris

• Article
  22 March 2022 | Open Access

  Exon skipping induced by CRISPR-directed gene editing regulates the response to chemotherapy in non-small cell lung carcinoma cells

  • Kelly Banas
  • , Shirin Modarai
  •  & Eric B. Kmiec

• Brief Communication
  04 March 2021 | Open Access

  Alternative oxidase encoded by sequence-optimized and chemically-modified RNA transfected into mammalian cells is catalytically active

  • Luca Giordano
  • , Manish K. Aneja
  •  & Marten Szibor

• Brief Communication | 20 March 2020

  ‘Mini’ U6 Pol III promoter exhibits nucleosome redundancy and supports multiplexed coupling of CRISPR/Cas9 effects

  • Roland Preece
  • , Christos Georgiadis
  •  & Waseem Qasim

• Article
  02 March 2020 | Open Access

  Nr2e3 is a genetic modifier that rescues retinal degeneration and promotes homeostasis in multiple models of retinitis pigmentosa

  • Sujun Li
  • , Shyamtanu Datta
  •  & Neena B. Haider

• Article | 11 December 2018

  Histone deacetylase inhibitors reactivate silenced transgene in vivo

  • Chunbo Zhang
  • , Guisheng Zhang
  •  & Dexi Liu

• Original Article | 20 April 2017

  Detailed comparison of retroviral vectors and promoter configurations for stable and high transgene expression in human induced pluripotent stem cells

  • D Hoffmann
  • , J W Schott
  •  & A Schambach

• Original Article | 17 April 2017

  Development of potent class II transactivator gene delivery systems capable of inducing de novo MHC II expression in human cells, in vitro and ex vivo

  • M L Palma
  • , P Duangkhae
  •  & E T A Marques

• Original Article | 10 March 2016

  Hair cell stereociliary bundle regeneration by espin gene transduction after aminoglycoside damage and hair cell induction by Notch inhibition

  • A Taura
  • , K Taura
  •  & A F Ryan

• Original Article | 14 July 2015

  Gene therapy with neurogenin3, betacellulin and SOCS1 reverses diabetes in NOD mice

  • R Li
  • , E Buras
  •  & L Chan

• Original Article | 29 January 2015

  Localizing the RPGR protein along the cilium: a new method to determine efficacies to treat RPGR mutations

  • R Da Costa
  • , E Glaus
  •  & J Neidhardt

• Original Article | 31 March 2011

  Inhibition of nuclear delivery of plasmid DNA and transcription by interferon γ: hurdles to be overcome for sustained gene therapy

  • L Zang
  • , M Nishikawa
  •  & Y Takakura

• Original Article | 10 March 2011

  A bidirectional promoter architecture enhances lentiviral transgenesis in embryonic and extraembryonic stem cells

  • M C Golding
  •  & M R W Mann