Featured
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Original Article |
Conditional control of suicide gene expression in tumor cells with theophylline-responsive ribozyme
- Y Zhang
- , J Wang
- & R Pei
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Original Article |
Identification of an alveolar type I epithelial cell-specific DNA nuclear import sequence for gene delivery
- L Gottfried
- , X Lin
- & D A Dean
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Original Article |
BTK gene targeting by homologous recombination using a helper-dependent adenovirus/adeno-associated virus hybrid vector
- H Yamamoto
- , M Ishimura
- & T Hara
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Enabling Technologies |
TALEN-mediated editing of endogenous T-cell receptors facilitates efficient reprogramming of T lymphocytes by lentiviral gene transfer
- B Berdien
- , U Mock
- & B Fehse
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Original Article |
Specific reactivation of latent HIV-1 with designer zinc-finger transcription factors targeting the HIV-1 5′-LTR promoter
- P Wang
- , X Qu
- & H Zhu
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Original Article |
Zinc-finger nuclease-mediated gene correction using single AAV vector transduction and enhancement by Food and Drug Administration-approved drugs
- B L Ellis
- , M L Hirsch
- & M H Porteus
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Original Article |
Self-complementary AAV mediates gene targeting and enhances endonuclease delivery for double-strand break repair
- M L Hirsch
- , L Green
- & R J Samulski
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Original Article |
rAAV2/5 gene-targeting to rods:dose-dependent efficiency and complications associated with different promoters
- W A Beltran
- , S L Boye
- & G D Aguirre
Deletion of the GAA repeats from the human frataxin gene using the CRISPR-Cas9 system in YG8R-derived cells and mouse models of Friedreich ataxia
Non-viral delivery of genome-editing nucleases for gene therapy
Progress and prospects: oligonucleotide-directed gene modification in mouse embryonic stem cells: a route to therapeutic application