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GENE THERAPY

Gene therapy goes the distance in Wiskott–Aldrich syndrome

Long-term follow-up data reinforce the curative potential of hematopoietic stem-cell gene therapy for this rare primary immunodeficiency disorder.

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Correspondence to Alessandra Biffi.

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Biffi, A. Gene therapy goes the distance in Wiskott–Aldrich syndrome. Nat Med 28, 24–25 (2022). https://doi.org/10.1038/s41591-021-01653-7

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  • DOI: https://doi.org/10.1038/s41591-021-01653-7

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