Gene therapy goes the distance in Wiskott–Aldrich syndrome

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Author information

Pediatric Hematology, Oncology and Stem Cell Transplant Division, Padua University Hospital, Padua, Italy
Alessandra Biffi
Gene Therapy Program, Dana Farber–Boston Children’s Cancer and Blood Disorders Center, Boston, MA, USA
Alessandra Biffi

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Alessandra Biffi
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Correspondence to Alessandra Biffi.

The author declares no competing interests.

Biffi, A. Gene therapy goes the distance in Wiskott–Aldrich syndrome. Nat Med 28, 24–25 (2022). https://doi.org/10.1038/s41591-021-01653-7