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GENE THERAPY

A plethora of gene therapies for hemoglobinopathies

CRISPR-Cas gene editing enters the field of promising clinical approaches for mitigating hemoglobin defects in patients with hemoglobinopathies.

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Fig. 1: Current gene therapies for hemoglobinopathies.

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Acknowledgements

C.E.D. is funded by the intramural program of the National Heart, Lung, and Blood Institute.

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Correspondence to Cynthia E. Dunbar.

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Dunbar, C.E. A plethora of gene therapies for hemoglobinopathies. Nat Med 27, 202–204 (2021). https://doi.org/10.1038/s41591-021-01235-7

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