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Their lives in their hands

A Publisher Correction to this article was published on 21 November 2019

This article has been updated

The devastating diagnosis of a rare disease is prompting an increasing number of people to go to the bench and take research into their own hands

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  • 21 November 2019

    An amendment to this paper has been published and can be accessed via a link at the top of the paper.


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Branca, M.A. Their lives in their hands. Nat Biotechnol 37, 1255–1260 (2019).

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