After a decade of unsuccessful attempts to correct one form of severe combined immunodeficiency using gene therapy, success has finally been achieved in another genetic type. Whether this success is due to the type of defect or to other factors, such as improved retroviral vectors or stem cell growth conditions, is not yet apparent.
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Buckley, R. Gene therapy for human SCID: Dreams become reality. Nat Med 6, 623–624 (2000). https://doi.org/10.1038/76185
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DOI: https://doi.org/10.1038/76185
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