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The cost of treating Gaucher disease

Nature Medicine volume 2, pages 523–524 (1996)Cite this article

Treatments fashioned specifically for rare diseases are necessarily very expensive. A fully satisfactory solution to this problem has not yet been found.

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  1. The Scripps Research Institute, 10666 North Torrey Pines Road, La Jolla, California, 92037, USA

    Ernest Beutler

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  1. Ernest Beutler
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Beutler, E. The cost of treating Gaucher disease. Nat Med 2, 523–524 (1996). https://doi.org/10.1038/nm0596-523

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