Genetic mutations are usually the source of debilitating disease. But, for a number of rare inherited blood and skin disorders, spontaneous DNA changes can repair and even reverse disease symptoms. Mike May explores the therapeutic potential of this 'natural gene therapy'.
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May, M. Mutations to the rescue. Nat Med 17, 405–407 (2011). https://doi.org/10.1038/nm0411-405
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DOI: https://doi.org/10.1038/nm0411-405
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