RNA metabolism articles within Gene Therapy

Featured

• Review Article
  02 June 2022 | Open Access

  Splicing mutations in the CFTR gene as therapeutic targets

  • Karine Deletang
  •  & Magali Taulan-Cadars

• Article | 12 June 2020

  miR-503-5p inhibits colon cancer tumorigenesis, angiogenesis, and lymphangiogenesis by directly downregulating VEGF-A

  • Linlin Wei
  • , Chaonan Sun
  •  & Shichen Sun

• Original Article | 07 December 2017

  Site-directed RNA editing by adenosine deaminase acting on RNA for correction of the genetic code in gene therapy

  • Md T A Azad
  • , S Bhakta
  •  & T Tsukahara

• Review | 09 May 2017

  How the discovery of ISS-N1 led to the first medical therapy for spinal muscular atrophy

  • N N Singh
  • , M D Howell
  •  & R N Singh