Genome articles within Gene Therapy

Featured

• Original Article | 27 June 2013

  Long-term efficacy of ciliary muscle gene transfer of three sFlt-1 variants in a rat model of laser-induced choroidal neovascularization

  • M El Sanharawi
  • , E Touchard
  •  & F Behar-Cohen

• Original Article | 01 December 2011

  Manipulation of mtDNA heteroplasmy in all striated muscles of newborn mice by AAV9-mediated delivery of a mitochondria-targeted restriction endonuclease

  • S R Bacman
  • , S L Williams
  •  & C T Moraes

• Enabling Technologies | 02 September 2010

  Use of human MAR elements to improve retroviral vector production

  • M Buceta
  • , J L Galbete
  •  & N Mermod

• Original Article | 11 March 2010

  Organ-specific shifts in mtDNA heteroplasmy following systemic delivery of a mitochondria-targeted restriction endonuclease

  • S R Bacman
  • , S L Williams
  •  & C T Moraes

• News and Commentary | 07 January 2010

  The battle to prevent the transmission of mitochondrial DNA disease: Is karyoplast transfer the answer?

  • J C St John
  •  & K H S Campbell