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Decision making on HSCT in patients with hemoglobinopathies; an EBMT Pediatric Diseases Working Party and Inborn Errors Working Party scenario-based survey on physicians’ perspectives

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Data are available from the authors upon reasonable request and with permission of the EBMT.


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We thank all respondents who participated in the survey.

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Authors and Affiliations



Conception and design of the work: HM, MV, AL, FS, AHP, and MHA. Data collection: HM, TS, and KK. Data analysis and interpretation: BM, HM, TS, JB, and FS. Drafting the article: HM, BM, MV, AL, and FS. Revision of the article: HM, BM, MV, AL, FS, AHP, TS, JB, KK, MHA, BN, and SC.

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Correspondence to Hilda Mekelenkamp.

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Mekelenkamp, H., de Vries, M., Markovitch, B. et al. Decision making on HSCT in patients with hemoglobinopathies; an EBMT Pediatric Diseases Working Party and Inborn Errors Working Party scenario-based survey on physicians’ perspectives. Bone Marrow Transplant (2023).

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