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Non Malignant Diseases

The controversial and changing role of haematopoietic cell transplantation for lysosomal storage disorders: an update

Bone Marrow Transplantation volume 41, pages S87–S89 (2008)Cite this article

Abstract

Haematopoietic cell transplantation (HCT) can benefit some selected subsets of patients with lysosomal diseases. Results had been impressive in children with MPS I-H, but poor in other disorders. Careful, multidisciplinary decision-making regarding whether to recommend HCT and how to provide optimal pre- and post-HCT care has proven essential to increase the likelihood of a good outcome.

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  1. Paediatric Department of Milano-Bicocca University, BMT Unit, San Gerardo Hospital, Monza, Italy

    A M Rovelli

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  1. A M Rovelli
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Correspondence to A M Rovelli.

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Rovelli, A. The controversial and changing role of haematopoietic cell transplantation for lysosomal storage disorders: an update. Bone Marrow Transplant 41 (Suppl 2), S87–S89 (2008). https://doi.org/10.1038/bmt.2008.62

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