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AAVant-garde gene therapy

Nature Medicine volume 5, pages 21–22 (1999)Cite this article

Abstract

Using a recombinant adeno-associated virus vector to deliver the factor IX gene, two groups achieve long-term partial correction of hemophilia B in a canine model of the disease (pages 56–70).

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Authors and Affiliations

  1. Institute for Gene Therapy and Molecular Medicine, Mount Sinai School of Medicine, New York, 10029, New York, USA

    R. Michael Linden & Savio L.C. Woo

Authors
  1. R. Michael Linden
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  2. Savio L.C. Woo
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Linden, R., Woo, S. AAVant-garde gene therapy. Nat Med 5, 21–22 (1999). https://doi.org/10.1038/4698

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