A new study shows that normalizing the number of CUG repeat–containing DMPK transcripts in a mouse model of myotonic dystrophy reverses the myotonia and cardiac conduction defects. This discovery suggests new therapeutic approaches for the disease.
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Timchenko, L. Reversal of fortune. Nat Genet 38, 976–977 (2006). https://doi.org/10.1038/ng0906-976
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DOI: https://doi.org/10.1038/ng0906-976
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