Gene therapy trials give mixed messages.
This is a preview of subscription content, access via your institution
Access options
Subscribe to this journal
Receive 51 print issues and online access
$199.00 per year
only $3.90 per issue
Buy this article
- Purchase on Springer Link
- Instant access to full article PDF
Prices may be subject to local taxes which are calculated during checkout
References
Daly, T.M. et al. Prevention of systemic clinical disease in MPS VII mice following AAV-mediated neonatal gene transfer. Gene Therapy 8, 1291 - 1298 (2001).
Song, S. et al. Stable therapeutic serum levels of human alpha-1 antitrypsin (AAT) after portal vein injection of recombinant adeno-associated virus (rAAV) vectors. Gene Therapy 8, 1299 - 1306 (2001).
Donsante, A. et al. Observed incidence of tumourigenesis in long-term rodent studies of rAAV vectors. Gene Therapy 8, 1343 - 1346 (2001).
Rights and permissions
About this article
Cite this article
Prevention of systemic clinical disease in MPS VII mice following AAV-mediated neonatal gene transfer. Nature (2001). https://doi.org/10.1038/news010906-13
Published:
DOI: https://doi.org/10.1038/news010906-13
