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Hematopoietic stem cell transplantation in childhood inherited bone marrow failure syndrome

Bone Marrow Transplantation volume 41, pages 127–132 (2008)Cite this article

Abstract

Aplastic anemia is a rare disease in children that is most commonly idiopathic and less often a hereditary disorder. Hereditary bone marrow failure (BMF) syndromes, however, should be considered both in children and in adults before any attempt at treatment. Precise diagnosis is important because it will modify prognostic treatment options and the results of bone marrow transplantation. In this review, we will report recent results of treatment of Fanconi anemia and other hereditary BMF syndromes.

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Authors and Affiliations

  1. Hematology Department, Eurocord Hôpital, Saint Louis, Paris, France

    E Gluckman

  2. Blood and Marrow Transplant Program, University of Minnesota, Minneapolis, MN, USA

    J E Wagner

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  1. E Gluckman
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  2. J E Wagner
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Correspondence to E Gluckman.

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Gluckman, E., Wagner, J. Hematopoietic stem cell transplantation in childhood inherited bone marrow failure syndrome. Bone Marrow Transplant 41, 127–132 (2008). https://doi.org/10.1038/sj.bmt.1705960

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