Showing 1–11 of 11 results
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Human adenylate kinase 2 deficiency causes a profound hematopoietic defect associated with sensorineural deafness
- Marina Cavazzana-Calvo and colleagues report mutations...
- Chantal Lagresle-Peyrou
- , Emmanuelle M Six
- , Capucine Picard
- , Frédéric Rieux-Laucat
- , Vincent Michel
- , Andrea Ditadi
- , Corinne Demerens-de Chappedelaine
- , Estelle Morillon
- , Françoise Valensi
- , Karen L Simon-Stoos
- , James C Mullikin
- , Lenora M Noroski
- , Céline Besse
- , Nicolas M Wulffraat
- , Alina Ferster
- , Manuel M Abecasis
- , Fabien Calvo
- , Christine Petit
- , Fabio Candotti
- , Laurent Abel
- , Alain Fischer
- & Marina Cavazzana-Calvo
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International AIDS Society global scientific strategy: towards an HIV cure 2016
- Steven G Deeks
- , Sharon R Lewin
- , Anna Laura Ross
- , Jintanat Ananworanich
- , Monsef Benkirane
- , Paula Cannon
- , Nicolas Chomont
- , Daniel Douek
- , Jeffrey D Lifson
- , Ying-Ru Lo
- , Daniel Kuritzkes
- , David Margolis
- , John Mellors
- , Deborah Persaud
- , Joseph D Tucker
- , Françoise Barre-Sinoussi
- , Galit Alter
- , Judith Auerbach
- , Brigitte Autran
- , Dan H Barouch
- , Georg Behrens
- , Marina Cavazzana
- , Zhiwei Chen
- , Éric A Cohen
- , Giulio Maria Corbelli
- , Serge Eholié
- , Nir Eyal
- , Sarah Fidler
- , Laurindo Garcia
- , Cynthia Grossman
- , Gail Henderson
- , Timothy J Henrich
- , Richard Jefferys
- , Hans-Peter Kiem
- , Joseph McCune
- , Keymanthri Moodley
- , Peter A Newman
- , Monique Nijhuis
- , Moses Supercharger Nsubuga
- , Melanie Ott
- , Sarah Palmer
- , Douglas Richman
- , Asier Saez-Cirion
- , Matthew Sharp
- , Janet Siliciano
- , Guido Silvestri
- , Jerome Singh
- , Bruno Spire
- , Jeffrey Taylor
- , Martin Tolstrup
- , Susana Valente
- , Jan van Lunzen
- , Rochelle Walensky
- , Ira Wilson
- & Jerome Zack
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Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
- Marina Cavazzana-Calvo
- , Emmanuel Payen
- , Olivier Negre
- , Gary Wang
- , Kathleen Hehir
- , Floriane Fusil
- , Julian Down
- , Maria Denaro
- , Troy Brady
- , Karen Westerman
- , Resy Cavallesco
- , Beatrix Gillet-Legrand
- , Laure Caccavelli
- , Riccardo Sgarra
- , Leila Maouche-Chrétien
- , Françoise Bernaudin
- , Robert Girot
- , Ronald Dorazio
- , Geert-Jan Mulder
- , Axel Polack
- , Arthur Bank
- , Jean Soulier
- , Jérôme Larghero
- , Nabil Kabbara
- , Bruno Dalle
- , Bernard Gourmel
- , Gérard Socie
- , Stany Chrétien
- , Nathalie Cartier
- , Patrick Aubourg
- , Alain Fischer
- , Kenneth Cornetta
- , Frédéric Galacteros
- , Yves Beuzard
- , Eliane Gluckman
- , Frederick Bushman
- , Salima Hacein-Bey-Abina
- & Philippe Leboulch