Impatient with the slow pace of clinical research, families of individuals suffering from untreatable diseases are taking matters into their own hands—with some success. Virginia Hughes reports.
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Hughes, V. When patients march in. Nat Biotechnol 28, 1145–1148 (2010). https://doi.org/10.1038/nbt1110-1145
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DOI: https://doi.org/10.1038/nbt1110-1145
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