Featured Content

During 2017, 2018, 2019 and 2020 we have been delighted to see Gene Therapy content included in a number of Springer Nature collections and campaigns, which contain content from across the Springer Nature portfolio and are a great way to not only showcase the great research that is being published in our journals, but bring wider attention to individual journals and introduce them to more readers. We are excited to see Gene Therapy content be included in more collections and campaigns in 2021 and encourage all to submit their papers to Gene Therapy too and have the opportunity to have their work showcased to Springer Nature's large and global audience.

2020 Global Year for the Prevention of Pain

Sigma-1 receptor activity in primary sensory neurons is a critical driver of neuropathic pain


Time-series oligonucleotide count to assign antiviral siRNAs with long utility fit in the big data era

Gene Therapy

An important step on the long path to clinical application of in utero gene therapy

Delivering efficient liver-directed AAV-mediated gene therapy

Gene therapy for spinomuscular atrophy: a biomedical advance, a missed opportunity for more equitable drug pricing

Developing gene and cell therapies for rare diseases: an opportunity for synergy between academia and industry

A brief account of viral vectors and their promise for gene therapy

World Aid's Day 2018

Current application of CRISPR/Cas9 gene-editing technique to eradication of HIV/AIDs

DNA Day 2018

Non-viral delivery of genome-editing nucleases for gene therapy

Targeted in vivo knock-inof human alpha-1-antitrypsin cDNA using adenoviral delivery of CRISPR/Cas9

INSR gene polymorphisms correlate with sensitivity to platinum-based chemotherapy and prognosis in patients with epithelial ovarian cancer

Telomerase-specific oncolytic adenovirus expressing TRAIL suppresses peritoneal dissemination of gastric cancer

Human genomics projects and precision medicine

In situ regeneration of retinol pigment epithelium by gene transfer of E2F2: a potential strategy for treatment of macular degenerations

A new plasmid-based microRNA inhibitor system that inhibits microRNA families in transgenic mice and cells: a potential new therapeutic reagent

Herpes virusMicroRNAs for use in gene therapy immune-evasion strategies

Precision Medicine

How the discovery of ISS-N1 led to the first medical therapy for spinal muscular atrophy

The clinical landscape for SMA in a new therapeutic era

DNA Day 2017

Live-cell imaging to compare the transfection and geen silencing efficiency of calcium phosphate nanoparticles and a liposomal transfection agent

Identification of an alveolar type I epithelial cell-specific DNA nuclear import sequence for gene delivery