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GENE THERAPY

Towards therapeutic base editing

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Base editors function in mouse fetuses and in the livers of adult mice to treat a genetic disorder.

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Fig. 1: Base editing can be applied therapeutically for metabolic disorders.

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Correspondence to Jin-Soo Kim.

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The authors declare no competing interests.

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Seo, H., Kim, JS. Towards therapeutic base editing. Nat Med 24, 1493–1495 (2018). https://doi.org/10.1038/s41591-018-0215-3

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