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Belzutifan: a novel therapy for von Hippel–Lindau disease

A recent clinical trial reports promising efficacy and safety data for belzutifan in patients with von Hippel–Lindau (VHL) disease–associated renal cell carcinoma. On the basis of these results, belzutifan became the first therapeutic agent to be approved for the systemic treatment of cancer associated with VHL disease.

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Correspondence to Kan Gong.

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Zhou, J., Gong, K. Belzutifan: a novel therapy for von Hippel–Lindau disease. Nat Rev Nephrol 18, 205–206 (2022).

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