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The authors are grateful to Graciana Diez-Roux (TIGEM Scientific Office) for the critical reading of the manuscript.
AA is funded by Fondazione Telethon, the European Research Council (ERC) (grant number 694323 “EYEGET”) and by the European Union Horizon 2020 and Marie Curie programs (grants number: 825825 “Upgrade” and 813490 “StarT”, respectively). IT receives funding from University of Naples Federico II, STAR Program.
Conflict of interest
IT, PT and AA are co-inventors on patents related to both dual AAV and AAV intein vectors.
Publisher’s note Springer Nature remains neutral with regard to jurisdictional claims in published maps and institutional affiliations.
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Trapani, I., Tornabene, P. & Auricchio, A. Large gene delivery to the retina with AAV vectors: are we there yet?. Gene Ther (2020). https://doi.org/10.1038/s41434-020-0174-4