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Venetoclax-based therapy as a bridge to allogeneic hematopoietic cell transplantation in children with relapsed/refractory AML

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Fig. 1: Key transplant outcomes.

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Authors and Affiliations



TP and SN conceived and designed the retrospective study. Patient enrollment and management: SEK, JER, RE, RM, EM, EO, AQ, A Sharma, A Srinivasan, A Suliman, ACT, MPV, and BMT. Analysis and interpretation of data: TP, SN, YL, and EA. Writing of the manuscript: TP, SN, BMT, and SG. Review/revision of the manuscript: all authors.

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Correspondence to Thomas Pfeiffer or Swati Naik.

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Competing interests

SG and MPV are a co-inventors on patent applications in the fields of cell or gene therapy for cancer. SG is a consultant of TESSA Therapeutics, a member of the Data and Safety Monitoring Board (DSMB) of Immatics, and has received honoraria from Tidal, Catamaran Bio, Sanofi, and Novartis within the last 2 years. Author A Sharma has received consultant fees from Spotlight Therapeutics, Medexus Inc. and Vertex Pharmaceuticals, has received research finding from CRISPR Therapeutics and honoraria from Vindico Medical Education. All other authors have no conflict of interest to disclose.

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Pfeiffer, T., Li, Y., Ashcraft, E. et al. Venetoclax-based therapy as a bridge to allogeneic hematopoietic cell transplantation in children with relapsed/refractory AML. Bone Marrow Transplant (2022).

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