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Hematopoietic stem cell transplantation for cytidine triphosphate synthase 1 (CTPS1) deficiency

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Correspondence to Zohreh Nademi.

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Nademi, Z., Wynn, R.F., Slatter, M. et al. Hematopoietic stem cell transplantation for cytidine triphosphate synthase 1 (CTPS1) deficiency. Bone Marrow Transplant 54, 130–133 (2019).

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