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Inserting optimism into gene therapy

A small clinical trial for an immunodeficiency disease provides a new way to think about gene therapy (pages 401–409).

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Figure 1: Gene-corrected neutrophils in the blood of an individual with CGD after HSPC gene therapy.

Katie Ris

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Naldini, L. Inserting optimism into gene therapy. Nat Med 12, 386–388 (2006). https://doi.org/10.1038/nm0406-386

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