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Preemptive therapy for genetic disease

Nature Medicine volume 2, pages 161162 (1996) | Download Citation

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In utero stem cell transplantation for inherited blood cell disorders.

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References

  1. 1.

    et al. Successful treatment of X-linked recessive severe combined immunodeficiency (X-SCID) by the in utero transplantation of CD34 enriched paternal bone marrow cells. Blood 86, 125a (1995).

  2. 2.

    et al. Development of immunity in human severe primary T cell deficiency following haploidentical bone marrow stem cell transplantation. J. Immunoi. 136, 2398–2407 (1986).

  3. 3.

    et al. Interleukin-2 receptor γ chain mutation results in X-linked severe combined immunodeficiency in humans. Cell 73, 147–157 (1993).

  4. 4.

    and In utero hematopoietic stem cell transplants for inherited diseases. Am. J. Pediat. Hematol. J. Oncol. 16, 35–42 (1994).

  5. 5.

    et al. Mixed chimerism in thalassemic patients after bone marrow transplantation. B.M.T. 10, 143–146 (1992).

  6. 6.

    et al. Analysis of β-globin mutations shows stable mixed chimerism in patients with thalassemia after bone marrow transplantation. Blood 86, 3241–3246 (1995).

  7. 7.

    et al. Marrow transplantation in patients with thalassemia responsive to chelation therapy N. Engl. J. Med. 329, 840–844 (1993).

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Author information

Affiliations

  1. Divisions of Hematology and Medical Genetics University of Washington Seattle, Washington, 98195, USA

    • C.Anthony Blau
    •  & George Stamatoyannopoulos

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DOI

https://doi.org/10.1038/nm0296-161

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