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Genetic therapy for spinal muscular atrophy

06 October 2022 Editor’s Note: readers are alerted that the primary research paper covered in this News & Views has been retracted.

A severe inherited neuromuscular disease is corrected in mice by intravenous gene delivery.

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Figure 1: Gene therapy for mice with spinal muscular atrophy (SMA).

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  • 06 October 2022

    Editor’s Note: readers are alerted that the primary research paper covered in this News & Views has been retracted.


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Correspondence to Alex MacKenzie.

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The author declares no competing financial interests.

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MacKenzie, A. Genetic therapy for spinal muscular atrophy. Nat Biotechnol 28, 235–237 (2010).

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