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Fooling Mother Nature

Correcting defective genes at the mRNA level shows promise for the treatment of cystic fibrosis.

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Figure 1: The use of trans-splicing to correct a hereditary disorder at the RNA level.

© Bob Crimi

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Crystal, R. Fooling Mother Nature. Nat Biotechnol 20, 32–33 (2002). https://doi.org/10.1038/nbt0102-32

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