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Worth the RISC?

The long, tortuous race to market a therapeutic based on RNA interference (RNAi) may be nearing its end. Ken Garber reports.

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Figure 1: siRNA therapies face many barriers to reaching their targets.

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Garber, K. Worth the RISC?. Nat Biotechnol 35, 198–202 (2017). https://doi.org/10.1038/nbt.3810

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