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Patching up hematopoietic stem cells

An approach for efficient genome editing in human hematopoietic stem cells could be useful in the treatment of immunological disorders.

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Figure 1: HDR-mediated gene insertion in HSCs as in Wang et al.1.

Marina Corral Spence/Nature Publishing Group


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Correspondence to Adrian J Thrasher.

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The authors declare no competing financial interests.

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Santilli, G., Thrasher, A. Patching up hematopoietic stem cells. Nat Biotechnol 33, 1236–1238 (2015).

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