A pharmacogenomic approach validates AG-221 as an effective and on-target therapy in IDH2 mutant AML

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This work was funded by project and program grants (RWJ and LMK) from the National Health and Medical Research Council of Australia (NHMRC) and a grant from the Peter Mac Foundation (LMK). RWJ was supported by an NHMRC Fellowship and LMK was supported by a Victorian Cancer Agency fellowship.

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Correspondence to L M Kats or R W Johnstone.

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Competing interests

RN and KEY are employees of and have ownership interest (including some with patents) in Agios Pharmaceuticals. The remaining authors declare no conflict of interest.

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Supplementary Information accompanies this paper on the Leukemia website

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