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Delivering efficient liver-directed AAV-mediated gene therapy

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JB is supported by a Clinical Starter Research Grant from Great Ormond Street Hospital for Children Charity.

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JB wrote the manuscript. SNW, IEA and PG contributed and revised the manuscript. All authors read and approved the final manuscript.

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Correspondence to J Baruteau.

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Baruteau, J., Waddington, S., Alexander, I. et al. Delivering efficient liver-directed AAV-mediated gene therapy. Gene Ther 24, 263–264 (2017).

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