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Experimental gene therapy frees ‘bubble-boy’ babies from a life of isolation

Treatment restores immune-system function in young children with severe disorder.
  1. Heidi Ledford
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An experimental gene therapy has restored functioning immune systems to seven young children with a severe disorder that would have sentenced them to a life of isolation to avoid potentially deadly infections. They are now with family at home, and an eighth child is slated to be released from hospital at the end of this week.

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doi: https://doi.org/10.1038/d41586-019-01257-9

References

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