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Translational medicine

Mice and men show the way

Disorders caused by single genes, such as fragile X syndrome, share symptoms with the genetically complex autism spectrum disorders. It emerges that effective drugs for the former may lead to therapies for the latter.

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Figure 1: From lab to clinic.


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Correspondence to Evdokia Anagnostou.

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Anagnostou, E. Mice and men show the way. Nature 491, 196–197 (2012).

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