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Hematopoietic cell transplantation for mucopolysaccharidosis IIB (Hunter syndrome); an ethical commentary

Bone Marrow Transplantation volume 25, pages 1097–1099 (2000)Cite this article

Abstract

Hunter syndrome is an X-linked metabolic storage disorder arising from deficiency of iduronate sulfatase enzyme activity. Despite the successful use of hematopoietic cell transplantation for a variety of lysosomal and peroxisomal storage diseases, limited benefit occurs following transplantation in either the severe or mild forms of Hunter syndrome. A brief ethical commentary is provided on the case of a boy with mucopolysaccharidosis IIB (ie the mild form) who received an unrelated umbilical cord blood transplant to improve his future quality of life. Bone Marrow Transplantation (2000) 25, 1097–1099.

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  1. Department of Pediatrics, University of Minnesota, Minneapolis, MN, USA

    C Peters & W Krivit

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Peters, C., Krivit, W. Hematopoietic cell transplantation for mucopolysaccharidosis IIB (Hunter syndrome); an ethical commentary. Bone Marrow Transplant 25, 1097–1099 (2000). https://doi.org/10.1038/sj.bmt.1702398

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