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TY  - JOUR
AU  - Sly, W.S.
AU  - Quinton, B.A.
AU  - McAlister, W.H.
AU  - Rimoin, D.L.
TI  - Beta glucuronidase deficiency: Report of clinical, radiologic, and biochemical features of a new mucopolysaccharidosis
JO  - J. Pediatr.
PY  - 1973///
VL  - 82
SP  - 249
EP  - 257
ER  - 

TY  - GEN
AU  - Neufeld, E.F.
AU  - Muenzer, J.
TI  - Metabolic Basis of Inherited Disease
PY  - 1995///
ER  - 

TY  - JOUR
AU  - Haskins, M.E.
AU  - Desnick, R.J.
AU  - DiFerrante, N.
AU  - Jezyk, P.F.
AU  - Patterson, D.F.
TI  - Beta-glucuronidase deficiency in a dog: A model of mucopolysaccharidosis VII
JO  - Pediatr. Res.
PY  - 1984///
VL  - 18
SP  - 980
EP  - 984
ER  - 

TY  - JOUR
AU  - Birkenmeier, E.H.
TI  - Murine mucopolysaccharidosis type VII: Characterization of a mouse with beta-glucuronidase deficiency
JO  - J. Clin. Invest.
PY  - 1989///
VL  - 83
SP  - 1258
EP  - 1256
ER  - 

TY  - GEN
AU  - Wolfe, J.H.
AU  - Sands, M.S.
TI  - Murine mucopolysaccharidosis type VII: A model system for somatic gene therapy of the central nervous system, in Protocols for Gene Transfer in Neuroscience: Towards Gene Therapy of Neurologic Disorders
PY  - 1996///
ER  - 

TY  - JOUR
AU  - Wolfe, J.H.
TI  - Reversal of pathology in murine mucopolysaccharidosis type VII by somatic cell gene transfer
JO  - Nature
PY  - 1992///
VL  - 360
SP  - 749
EP  - 753
M3  - 10.1038/360749a0
N1  - 10.1038/360749a0
UR  - http://dx.doi.org/10.1038/360749a0
ER  - 

TY  - JOUR
AU  - Wolfe, J.H.
AU  - Deshmane, S.L.
AU  - Fraser, N.W.
TI  - Herpesvirus vector gene transfer and expression of beta-glucuronidase in the central nervous system of MPS VII mice
JO  - Nature Genet.
PY  - 1992///
VL  - 1
SP  - 379
EP  - 384
ER  - 

TY  - JOUR
AU  - Moullier, P.
AU  - Bohl, D.
AU  - Heard, J.-M.
AU  - Danos, O.
TI  - Correction of lysosomal storage in the liver and spleen of MPS VII mice by implantation of genetically modified skin fibroblasts
JO  - Nature Genet.
PY  - 1993///
VL  - 4
SP  - 154
EP  - 159
ER  - 

TY  - JOUR
AU  - Sands, M.S.
TI  - Enzyme replacement therapy for murine mucopolysaccharidosis type VII
JO  - J. Clin. Invest
PY  - 1994///
VL  - 93
SP  - 2324
EP  - 2331
ER  - 

TY  - JOUR
AU  - Snyder, E.Y.
AU  - Taylor, R.M.
AU  - Wolfe, J.H.
TI  - Neural progenitor cell engraftment corrects lysosomal storage throughout the MPS VII mouse brain
JO  - Nature
PY  - 1995///
VL  - 374
SP  - 367
EP  - 370
M3  - 10.1038/374367a0
N1  - 10.1038/374367a0
UR  - http://dx.doi.org/10.1038/374367a0
ER  - 

TY  - GEN
AU  - Scriver, C.R.
AU  - Beaudet, A.L.
AU  - Sly, W.S.
AU  - Valle, D.
TI  - Metabolic Basis of Inherited Disease
PY  - 1995///
ER  - 

TY  - JOUR
AU  - Taylor, R.M.
AU  - Wolfe, J.H.
TI  - Cross-correction of beta-glucuronidase deficiency by retroviral vector-mediated gene transfer
JO  - Exp. Cell Res.
PY  - 1994///
VL  - 214
SP  - 606
EP  - 613
M3  - 10.1006/excr.1994.1298
N1  - 10.1006/excr.1994.1298
UR  - http://dx.doi.org/10.1006/excr.1994.1298
ER  - 

TY  - JOUR
AU  - Wolfe, J.H.
TI  - High level expression and export of beta-glucuronidase from murine mucopolysaccharidosis VII cells corrected by a double-copy retrovirus vector
JO  - Gene Ther.
PY  - 1995///
VL  - 2
SP  - 70
EP  - 78
ER  - 

TY  - JOUR
AU  - Fisher, L.J.
AU  - Gage, F.H.
TI  - Grafting in the mammalian central nervous system
JO  - Physiol. Rev.
PY  - 1993///
VL  - 73
SP  - 583
EP  - 616
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TY  - JOUR
AU  - Flanagan, J.R.
TI  - Cloning of a negative transcription factor that binds to the upstream conserved region of Moloney murine leukemia virus
JO  - Mol. Cell. Biol.
PY  - 1992///
VL  - 12
SP  - 38
EP  - 44
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TY  - JOUR
AU  - Ohashi, T.
TI  - Efficient transfer and sustained high expression of the human glucocerebrosidase gene in mice and their functional macrophages following transplantation of bone marrow transduced by a retroviral vector
JO  - Proc. Natl. Acad. Sci. USA
PY  - 1992///
VL  - 89
SP  - 11332
EP  - 11336
ER  - 

TY  - JOUR
AU  - Wolfe, J.H.
TI  - Restoration of normal lysosomal function in mucopolysaccharidosis type VII cells by gene transfer
JO  - Proc. Natl. Acad. Sci. USA
PY  - 1990///
VL  - 87
SP  - 2877
EP  - 2881
ER  - 

TY  - JOUR
AU  - Kyle, J.W.
TI  - Correction of murine mucopolysaccharidosis VII by a human [beta]-glucuronidase transgene
JO  - Proc. Natl. Acad. Sci. USA
PY  - 1990///
VL  - 87
SP  - 3914
EP  - 3918
ER  - 

TY  - JOUR
AU  - Taylor, R.M.
AU  - Wolfe, J.H.
TI  - Glycosaminoglycan storage in neonatal murine mucopolysaccharidosis type VII neurogltal cells and correction by |[beta]-glucuronidase gene transfer
JO  - J. Neurochem.
PY  - 1997///
VL  - 68
SP  - 2079
EP  - 2085
ER  - 

