Nature Medicine10, 816 - 820 (2004)
Published online: 4 July 2004; | doi:10.1038/nm1076
RNAi suppresses polyglutamine-induced neurodegeneration in a model of spinocerebellar ataxia
Haibin Xia, Qinwen Mao, Steven L Eliason, Scott Q Harper, Inês H Martins, Harry T Orr, Henry L Paulson, Linda Yang, Robert M Kotin
& Beverly L Davidson