Nature Medicine
1, 307 - 308 (1995)
doi:10.1038/nm0495-307
Sickle cell paths converge on hydroxyureaOrah S. Platt1
1Children's Hospital, Harvard Medical School, Boston, Massachusetts 02115, USA The realization that a mutation in a haemoglobin gene is at the root of sickle cell anaemia and the discovery of an effective treatment are separated by years. But sickle cell research is a model for how different paths of inquiry can come together with good result.
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