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Letter

Nature Genetics 35, 165–170 (1 October 2003) | doi:10.1038/ng1241

A novel ubiquitin ligase is deficient in Fanconi anemia

Amom Ruhikanta Meetei , Johan P de Winter , Annette L Medhurst , Michael Wallisch , Quinten Waisfisz , Henri J van de Vrugt , Anneke B Oostra , Zhijiang Yan , Chen Ling , Colin E Bishop , Maureen E Hoatlin , Hans Joenje & Weidong Wang

Fanconi anemia is a recessively inherited disease characterized by congenital defects, bone marrow failure and cancer susceptibility. Cells from individuals with Fanconi anemia are highly sensitive to DNA-crosslinking drugs, such as mitomycin C (MMC).