Kathryn L. Berrier MS, CGC, Zoheb B. Kazi MBBS, Sean N. Prater MD, MRes, Deeksha S. Bali PhD, Jennifer Goldstein PhD, CGC, Mihaela C. Stefanescu BS, Catherine W. Rehder PhD, Eleanor G. Botha MS, CGC, Carolyn Ellaway MBBS, PhD, Kaustuv Bhattacharya MD, Anna Tylki-Szymanska MD, PhD, Nesrin Karabul MD, Amy S. Rosenberg MD and Priya S. Kishnani MD

Genet Med advance online publication, March 5, 2015; doi:10.1038/gim.2015.6

In the published version of this article, Dr. Rosenberg’s name was misspelled.

In addition, in the first paragraph of the results section, the second sentence was incorrect.

“From this group, 23 CN patients with IPD were excluded from analysis because ITI treatment was administered in the naive setting; for 15 other CN patients with IPD, death occurred before 6 months on ERT or there were insufficient follow-up data; thus the resulting data analysis included 20 CN patients with IPD.”

should have been

“From this group, 23 CN patients with IPD were excluded from analysis because ITI treatment was administered in the naive setting; for 15 other CN patients with IPD, death occurred within 6 months on ERT or there were insufficient follow-up data; thus the resulting data analysis included 20 CN patients with IPD.” [Emphasis added]

The authors regret the errors.