Skip to main content

Thank you for visiting nature.com. You are using a browser version with limited support for CSS. To obtain the best experience, we recommend you use a more up to date browser (or turn off compatibility mode in Internet Explorer). In the meantime, to ensure continued support, we are displaying the site without styles and JavaScript.

  • News
  • Published:

Gene therapy hope for cystic fibrosis

SMaRT treatment for fatal disease shows promise.

This is a preview of subscription content, access via your institution

Access options

Buy this article

Prices may be subject to local taxes which are calculated during checkout

References

  1. Liu, X. et al. Partial correction of endogenous F508 CFTR in human cystic fibrosis airway epithelia by spliceosome-mediated RNA trans-splicing. Nature Biotechnology 20, 47 - 52 (2002).

    Article  Google Scholar 

Download references

Authors

Related links

Related links

Related links in Nature Research

Human gene therapy

Rights and permissions

Reprints and permissions

About this article

Cite this article

Thomson, J. Gene therapy hope for cystic fibrosis. Nature (2002). https://doi.org/10.1038/news020101-6

Download citation

  • Published:

  • DOI: https://doi.org/10.1038/news020101-6

Search

Quick links

Nature Briefing

Sign up for the Nature Briefing newsletter — what matters in science, free to your inbox daily.

Get the most important science stories of the day, free in your inbox. Sign up for Nature Briefing